Researchers from University of Pennsylvania and Children’s Hospital of Philadelphia continue to present hopeful results from gene therapy for leukemia three years after starting clinical trials.
gene therapy
Gene Therapy Shows Promise for Treating Hemophilia
Despite the vast promise of the genetic revolution in medicine, the fact remains that the hype has far outpaced the reality. Experiments with gene therapy, for instance, in which a new or corrected version of missing or damaged …
A treatment for blindness reveals the incredible plasticity of the brain
Recently doctors began gene-therapy trials to treat Leber’s congenital amaurosis, a common cause of blindness in babies and children. Now, a group of doctors reports that they’ve found an unexpected benefit of the gene therapy. After treatment, vision may continue to improve with time — because the brain can re-wire itself to better …